Society of Regenerative Sciences (India)

(Formerly known as Stem Cell Society (India))

Event Registration Membership Form

International Publications On Muscular Dystrophy

Muscular Dystrophy Publications International

  1. Taylor M, Jefferies J, Byrne B, Lima J, Ambale-Venkatesh B, Ostovaneh MR, Makkar R, Goldstein B, Smith RR, Fudge J, Malliaras K, Fedor B, Rudy J, Pogoda JM, Marbán L, Ascheim DD, Marbán E, Victor RG. Cardiac and skeletal muscle effects in the randomized HOPE-Duchenne trial. Neurology. 2019 Feb 19;92(8):e866-e878. doi: 10.1212/WNL.0000000000006950. Epub 2019 Jan 23. PmiD: 30674601; PMCID: PMC6396968.
  2. Li P, Cui K, Zhang B, Wang Z, Shen Y, Wang X, Zhang J, Tong F, Li S. Transplantation of human umbilical cord-derived mesenchymal stems cells for the treatment of Becker muscular dystrophy in affected pedigree members. International journal of molecular medicine. 2015 Apr 1;35(4):1051-7.
  3. Cossu G, Previtali SC, Napolitano S, Cicalese MP, Tedesco FS, Nicastro F, Noviello M, Roostalu U, Sora MG, Scarlato M, De Pellegrin M. Intra‐arterial transplantation of HLA‐matched donor mesoangioblasts in Duchenne muscular dystrophy. EMBO molecular medicine. 2015 Dec 1;7(12):1513-28.
  4. Skuk D, Roy B, Goulet M, Chapdelaine P, Bouchard JP, Roy R, Dugré FJ, Lachance JG, Deschênes L, Senay H, Sylvain M. Dystrophin expression in myofibers of Duchenne muscular dystrophy patients following intramuscular injections of normal myogenic cells. Molecular Therapy. 2004 Mar 1;9(3):475-82.
  5. Torrente Y, Belicchi M, Marchesi C, D'antona G, Cogiamanian F, Pisati F, Gavina M, Giordano R, Tonlorenzi R, Fagiolari G, Lamperti C. Autologous transplantation of muscle-derived CD133+ stem cells in Duchenne muscle patients. Cell transplantation. 2007 Jul;16(6):563-77.
  6. Law PK, Goodwin TG, Fang Q, Chen M, Li HJ, Florendo JA, Dana S, Kirby BS. Myoblast transfer therapy for Duchenne muscular dystrophy. Pediatrics International. 1991 Apr;33(2):206-15.
  7. Tremblay JP, Malouin F, Roy R, Huard J, Bouchard JP, Satoh A, Richards CL. Results of a triple blind clinical study of myoblast transplantations without immunosuppressive treatment in young boys with Duchenne muscular dystrophy. Cell transplantation. 1993 Mar;2(2):99-112.
  8. Klimczak A, Zimna A, Malcher A, Kozlowska U, Futoma K, Czarnota J, Kemnitz P, Bryl A, Kurpisz M. Co-Transplantation of Bone Marrow-MSCs and Myogenic Stem/Progenitor Cells from Adult Donors Improves Muscle Function of Patients with Duchenne Muscular Dystrophy. Cells. 2020 Apr 30;9(5):1119. doi: 10.3390/cells9051119. PmiD: 32365922; PMCID: PMC7290387.
  9. Duzhar VM, Radchenko VV, Gozhenko AI, Badiuk NS. Duchenne muscular dystrophy: treatment with fetal progenitor cell transplant.
  10. Dai A, Baspinar O, Yeşilyurt A, Sun E, Aydemir Çİ, Öztel ON, Capkan DU, Pinarli F, Agar A, Karaöz E. Efficacy of stem cell therapy in ambulatory and nonambulatory children with Duchenne muscular dystrophy - Phase I-II. Degener Neurol Neuromuscul Dis. 2018 Oct 26;8:63-77.
  11. Zhang C, Feng HY, Huang SL, Fang JP, Xiao LL, Yao XL, Chen C, Ye X, Zeng Y, Lu XL, Wen JM, Zhang WX, Li Z, Feng SW, Xu HG, Huang K, Zhou DH, Chen W, Xie YM, Xi J, Zhang M, Li Y, Liu Y. [Therapy of Duchenne muscular dystrophy with umbilical cord blood stem cell transplantation]. Zhonghua Yi Xue Yi Chuan Xue Za Zhi. 2005 Aug;22(4):399-405. Chinese. PmiD: 16086277.
  12. Kang PB, Lidov HG, White AJ, Mitchell M, Balasubramanian A, Estrella E, Bennett RR, Darras BT, Shapiro FD, Bambach BJ, Kurtzberg J, Gussoni E, Kunkel LM. Inefficient dystrophin expression after cord blood transplantation in Duchenne muscular dystrophy. Muscle Nerve. 2010 Jun;41(6):746-50.
  13. Taglietti V, Kefi K, Rivera L, Bergiers O, Cardone N, Coulpier F, Gioftsidi S, Drayton-Libotte B, Hou C, Authier F, Pietri-Rouxel F, Robert M, Bremond-Gignac D, Bruno C, Fiorillo C, Malfatti E, Lafuste P, Tiret L, Relaix F. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine. 2023;15(685).
  14. Takenaka-Ninagawa N, Goto M, Yoshioka CKB, Miki M, Sakurai H. Cell therapy for Duchenne muscular dystrophy using induced pluripotent stem cell-derived muscle stem cells and the potential of regenerative rehabilitation. Current Opinion in Biomedical Engineering. 2024;30:100523.
  15. Lee J, Park SE, Kim M, Kim H, Kwon J, Jeon HB, Chang JW, Lee J. Safety and tolerability of Wharton’s Jelly-Derived mesenchymal stem cells for patients with Duchenne muscular dystrophy: a Phase 1 clinical study. Journal of Clinical Neurology. 2025;21(1):40.
  16. Ebert AD, Yu J, Rose FF, Mattis VB, Lorson CL, Thomson JA, Svendsen CN. Induced pluripotent stem cells from a spinal muscular atrophy patient. Nature. 2008;457(7227):277–280.