Sharifzadeh N, Ghasemi A, Tavakol Afshari J, Moharari F, Soltanifar A, Talaei A, Pouryousof HR, Nahidi M, Fayyazi Bordbar MR, Ziaee M. Intrathecal autologous bone marrow stem cell therapy in children with autism: A randomized controlled trial. Asia Pac Psychiatry. 2021 Jun;13(2):e12445.
Dawson G, Sun JM, Baker J, Carpenter K, Compton S, Deaver M, Franz L, Heilbron N, Herold B, Horrigan J, et al. A Phase II randomized clinical trial of the safety and efficacy of intravenous umbilical cord blood infusion for treatment of children with autism spectrum disorder. J Pediatr. 2020;222:164–173.e5.
Chez M, Lepage C, Parise C, Dang-Chu A, Hankins A, Carroll M. Safety and observations from a placebo-controlled, crossover study to assess use of autologous umbilical cord blood stem cells to improve symptoms in children with autism. Stem Cells Transl Med. 2018;7(4):333-341.
Price J. Cell therapy approaches to autism: a review of clinical trial data. Mol Autism. 2020;11:37.
Lv YT, Zhang Y, Liu M, Qiuwaxi JN, Ashwood P, Cho SC, Huan Y, Ge RC, Chen XW, Wang ZJ, Kim BJ, Hu X. Transplantation of human cord blood mononuclear cells and umbilical cord-derived mesenchymal stem cells in autism. J Transl Med. 2013;11:196.
Villarreal-Martínez L, González-Martínez G, Sáenz-Flores M, Bautista-Gómez AJ, González-Martínez A, Ortiz-Castillo M, Robles-Sáenz DA, Garza-López E. Stem cell therapy in the treatment of patients with autism spectrum disorder: a systematic review and meta-analysis. Stem Cell Rev Rep. 2022;18(1):155-164.
Qu J, Liu Z, Li L, Zou Z, He Z, Zhou L, Luo Y, Zhang M, Ye J. Efficacy and safety of stem cell therapy in children with autism spectrum disorders: a systematic review and meta-analysis. Front Pediatr. 2022;10:897398.
Adnan M, Motiwala F, Trivedi C, et al. Human umbilical cord blood infusions in the management of autism spectrum disorder. Prim Care Companion CNS Disord. 2022;24(3):21r03042.
Paprocka J, Kaminiów K, Kozak S, Sztuba K, Emich-Widera E. Stem cell therapies for cerebral palsy and autism spectrum disorder: a systematic review. Brain Sci. 2021;11(12):1606.
Bradstreet JJ, Sych N, Antonucci N, Klunnik M, Ivankova O, Matyashchuk I, Demchuk M, Siniscalco D. Efficacy of fetal stem cell transplantation in autism spectrum disorders: an open-labeled pilot study. Cell Transplant. 2014;23 Suppl 1:S105-12.
Dawson G, Sun JM, Davlantis KS, Murias M, Franz L, Troy J, Simmons R, Sabatos-DeVito M, Durham R, Kurtzberg J. Autologous cord blood infusions are safe and feasible in young children with autism spectrum disorder: results of a single-center phase I open-label trial. Stem Cells Transl Med. 2017;6(5):1332-1339.
Carpenter KLH, Major S, Tallman C, Chen LW, Franz L, Sun J, Kurtzberg J, Song A, Dawson G. White matter tract changes associated with clinical improvement in an open-label trial assessing autologous umbilical cord blood for treatment of young children with autism. Stem Cells Transl Med. 2019;8(2):138-147.
Nguyen Thanh L, Nguyen HP, Ngo MD, Bui VA, Dam PTM, Bui HTP, Ngo DV, Tran KT, Dang TTT, Duong BD, Nguyen PAT, Forsyth N, Heke M. Outcomes of bone marrow mononuclear cell transplantation combined with interventional education for autism spectrum disorder. Stem Cells Transl Med. 2021;10(1):14-26.
Kobinia GS, Zaknun JJ, Pabinger C, Laky B. Autologous bone marrow-derived intrathecal stem cell transplant for autistic children: report of four cases and literature review. Front Pediatr. 2021;9:620188.
Lee SY, Ahn H, Jung WJ, Ahn J, Lee KH. A case study on autism spectrum disorder treatment using allogenic mesenchymal stem cells derived from the human umbilical cord. Case Rep Open Access. 2020;5:1-7.
Villarreal-Martinez L, MartÍnez-Garza LE, Rodriguez-Sanchez IP, Alvarez-Villalobos N, Guzman-Gallardo F, Pope-Salazar S, Salinas-Silva C, Cepeda-Cepeda MG, Garza-Bedolla A, Dominguez-Varela IA, et al. Correlation between CD133+ stem cells and clinical improvement in patients with autism spectrum disorders treated with intrathecal bone marrow-derived mononuclear cells. Innov Clin Neurosci. 2022;19(4-6):78-86.
Maric DM, Papic V, Radomir M, Stanojevic I, Sokolovac I, Milosavljevic K, Maric DL, Abazovic D. Autism treatment with stem cells: a case report. Eur Rev Med Pharmacol Sci. 2020;24(15):8075-8080.
Saisa D, Pradhani A, Shen JC, Atthariq MR, Khodavian W, Pawitan JA. Hematopoietic stem cell therapy in improving clinical outcomes for children with autism spectrum disorder: a systematic review and meta-analysis. Regen Eng Transl Med. 2024.
Akhtar M, Nashwan AJ. Evaluating Wharton’s jelly-derived stem cell therapy in autism: insights from a case study. World J Methodol. 2024;15(2).
Aa S, Sg S, Ig M, Mo K, Mp D, Ov I, Oo H, Ia S, Mv S, Dv V, Ki S. Clinical case of successful therapy for the patient with autism by use of fetal stem cells. J Stem Cell Ther Transplant. 2024;8(1):048–053.
Nguyen LT, Nguyen PM, Nguyen H, Bui HT, Dao LTM, Van Pham M, Hoang CK, Nguyen PT, Nguyen TTP, Nguyen ATP, Hoang VT, Bui HTP, Vuong NK, Van Ngo D. Outcomes of autologous bone marrow mononuclear cell administration combined with educational intervention in the treatment of autism spectrum disorder: a randomized, open-label, controlled phase II clinical trial. Stem Cell Res Ther. 2025;16(1).
Nie L, Irwin C, Geahchan S, Singh KK. Human pluripotent stem cell-derived models for autism spectrum disorder drug discovery. Expert Opin Drug Discov. 2024:1–19.
Wong CM, Tan CS, Riard N, Padmini YS, Daniel LM, Prasath A, Tan AM, Tan TC, Sultana R, Lam JCM. Autologous umbilical cord blood infusion for the treatment of autism in young children: a within-subjects open-label study on safety and efficacy. Autism Res. 2024;17(8):1721–1734.
Kabatas S, Civelek E, Savrunlu EC, Karaaslan U, Yıldız Ö, Karaöz E. Advances in the treatment of autism spectrum disorder: Wharton jelly mesenchymal stem cell transplantation. World J Methodol. 2024;15(1).
Wikarska A, Roszak K, Roszek K. Mesenchymal stem cells and purinergic signaling in autism spectrum disorder: bridging the gap between cell-based strategies and neuro-immune modulation. Biomedicines. 2024;12(6):1310.
Gesundheit B, Hochbaum L, Fetyukhina A, Vorobyev V, Vorobyev N. Mesenchymal stromal cell treatment alleviates autism spectrum disorder symptoms: a case report. Cureus. 2025.
Shamim S, Khan N, Greene DL, Habiba UE, Umer A. The promise of autologous and allogeneic cellular therapies in the clinical trials of autism spectrum disorder. Regen Med. 2023;18(4):347–361.